Matos, L., Gonçalves, M., Santos, J. I., Coutinho, M. F., Prata, M. J., Pires, M. J., . . . Alves, S. (2022). Antisense oligonucleotide exon-skipping as a therapeutic approach for Mucolipidosis type II a/b: In vitro and in vivo studies.

Matos, Liliana, Mariana Gonçalves, Juliana Inês Santos, Maria Francisca Coutinho, Maria João Prata, Maria João Pires, Paula Oliveira, and Sandra Alves. Antisense Oligonucleotide Exon-skipping as a Therapeutic Approach for Mucolipidosis Type II A/b: In Vitro and in Vivo Studies. 2022.

Matos, Liliana, et al. Antisense Oligonucleotide Exon-skipping as a Therapeutic Approach for Mucolipidosis Type II A/b: In Vitro and in Vivo Studies. 2022.