Targeted RNA-based therapies for Mucopolysaccharidosis

Over the last years, most of our work has been focused on the development of alternative, RNAbased therapies for a number of Lysosomal Storage Disorders (LSD), being Mucopolysaccharidosis (MPS) one of the most relevant. Currently, there are two major research lines being pursued: the first relies on...

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Detalhes bibliográficos
Autor principal: Santos, Juliana Inês (author)
Outros Autores: Gonçalves, Mariana (author), Matos, Liliana (author), Gaspar, Paulo (author), Pires, Maria João (author), Oliveira, Paula (author), Prata, Maria João (author), Coutinho, Maria Francisca (author), Alves, Sandra (author)
Formato: conferenceObject
Idioma:eng
Publicado em: 2022
Assuntos:
Mucopolissacaridoses
Doenças Lisossomais de Sobrecarga
Terapias de RNA
Genética Humana
Doenças Genéticas
Texto completo:http://hdl.handle.net/10400.18/8146
País:Portugal
Oai:oai:repositorio.insa.pt:10400.18/8146

Texto Completo

http://hdl.handle.net/10400.18/8146

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