Genetically Modulated Substrate Reduction Therapy for Sanfilippo Syndrome: Proof of Principle

About proof of principle in genetically modulated substrate reduction therapy for Sanfilippo syndrome.

Bibliographic Details
Main Author: Santos, Juliana Inês (author)
Other Authors: Coutinho, Maria Francisca (author), Gaspar, Paulo (author), Alves, Sandra (author)
Format: conferenceObject
Language:eng
Published: 2019
Subjects:
Lysosomal Storage Diseases
Mucopilysaccharidoses
Substrate Reduction Therapy
RNAi
Doenças Genéticas
Genética Humana
Online Access:http://hdl.handle.net/10400.18/6288
Country:Portugal
Oai:oai:repositorio.insa.pt:10400.18/6288

Internet

http://hdl.handle.net/10400.18/6288

Similar Items